Born deaf, little girl regains hearing thanks to gene therapy
In the United Kingdom, a one-and-a-half-year-old deaf girl is the youngest child to receive gene therapy, which allowed her to ...
Read moreTag: genetical therapy
Hereditary angioedema: DNA editing treatment cures genetic disease
A new therapy based on the CRISPR-Cas9 genetic scissors makes almost all seizures disappear in patients with hereditary angioedema, a ...
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Spinal muscular atrophy: “Gene therapy is a real magic potion!”
Lucie was diagnosed with a rare neuromuscular disease four months after her birth: spinal muscular atrophy type 1. This pathology ...
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Thanks to a new treatment, a deaf child hears for the first time
In the United States, a boy who has been deaf since birth regained his hearing after benefiting from gene therapy. ...
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Telethon: what is gene therapy?
On the occasion of the Telethon, Serge Braun, scientific director of the AFM-Téléthon, explains to us what gene therapy is. ...
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Deafness: 4 children regain hearing thanks to gene therapy
For the first time, a clinical trial of gene therapy has restored hearing in four children suffering from deafness. THE ...
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Blood diseases: gene therapy approved in the UK
The British medicines regulator has authorized a new gene therapy against two blood diseases, based on the patient's own cells: ...
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Bad cholesterol: gene therapy shows promise
A treatment using a gene therapy infusion helps reduce bad cholesterol in people at high risk of early heart attack ...
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Myotubular myopathy: the hope of gene therapy for children
Gene therapy has shown promising results in treating cases of myotubular myopathy, a rare disease that affects the muscles of ...
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Parkinson’s disease: hope for a new treatment thanks to gene therapy
Chinese researchers have designed a gene therapy that can reduce the symptoms associated with Parkinson's disease. THE ESSENTIAL Parkinson's disease ...
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Will gene therapy be able to overcome AIDS?
Gene therapy, combined with CRISPR technology, could make it possible to eliminate the AIDS virus from the organism of infected ...
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Deafness: gene therapy could reverse hearing loss
Researchers at Mass Eye and Ear Hospital have developed a gene therapy that could reverse hearing loss. THE ESSENTIAL Researchers ...
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Hair loss: what if gene therapy could treat alopecia?
An international group of researchers has developed an injectable treatment that could stimulate hair growth and thus fight against baldness. ...
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Color blindness: gene therapy to revive colors?
Thanks to the insertion of correcting genes in the retina, the function of the cones, responsible for color vision, was ...
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Gene therapy, a new treatment for haemophilia?
The results of a phase 2 clinical trial using gene therapy as a treatment for hemophilia are promising. Explanations. THE ...
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Age-related hearing loss: towards more effective screening
The identification of ten new genetic markers should make it possible to predict a risk of reduced hearing quality with ...
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Fatty liver disease: the identification of an RNA modification, the key to gene therapy
Hepatic steatosis or "fatty liver disease" could be prevented or slowed down by a chemical modification of certain RNA molecules. ...
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Gene therapy: the hope of treating a rare genetic disease in children
Young patients with Aromatic Amino Acid Decarboxylase deficiency, a rare pediatric genetic disease, may soon be treated with gene therapy. ...
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How RNA could repair DNA: an unexpected discovery
Human cells would be able to convert RNA sequences back into DNA, a function never identified until now. THE ESSENTIAL ...
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Congenital deafness: gene therapy, a promising way to regain hearing
Birth deafness is linked to mutations in a gene, otoferlin. For gene therapy to be effective, it must be associated ...
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Childhood blindness: gene therapy improves the sight of several children
The injection of copies of a missing gene that causes partial or total vision loss at birth or in early ...
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A promising therapy for Duchenne Muscular Dystrophy
A first child has started to receive treatment as part of the gene therapy trial conducted by the Téléthon laboratory. ...
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A new gene therapy for eye diseases
Researchers at Trinity College Dublin have just developed a new gene therapy approach that offers hope of one day curing ...
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Gene therapy: a little girl treated in a clinical study dies in the United States
Suffering from a rare and incurable pediatric disease, the little patient had received gene therapy treatment several months ago as ...
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Gene therapy: researchers have found a way to bypass the immune system
The CRISPR-Cas9 molecule is used for gene therapies… But it could also be used to control the body's immune response, ...
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Gene therapy, a hope for serious illnesses
Gene therapy, which consists of introducing genetic material to "correct" a patient's cells, would make it possible to treat serious ...
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A blind patient could regain his sight thanks to the “genetic scissors”
This is a “first”: hitherto tested in the laboratory, the CRISPR system known as “genetic scissors” was used on a ...
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Hemophilia A: a new gene treatment offers hope to patients
British researchers have just developed a revolutionary gene treatment for people suffering from hemophilia A. According to their first trials, ...
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Telethon: a man recovers his sight thanks to donations
The Telethon, which has been collecting donations for 30 years, supports research in gene therapy, which makes it possible to ...
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Cancer: the activity of CAR-T cells monitored using imaging
Researchers have managed to "tag" CAR-T cells reintroduced into patients with molecular markers to better understand their functioning and monitor ...
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